GNT0004
unknown (auto-discovered: gene-epigenetic-therapy)
Also known as: rAAV2/8-Spc5-12-hMD1
Classification
GeneTherapy
Regulatory Status
investigational; registered trials: NCT07856329 (PHASE2/PHASE3)
Unofficial source
Sources
1
Review
pending review
Overview
Unknown — GNT0004 was found by open discovery on 2026-10-26 and has not been researched yet.
Evidence and limitations
Known
n/a
Unknown
- Mechanism, dosing, safety, interactions and efficacy are unknown until research runs on this auto-discovered draft.
Study details: trial conditions, not guidance
These are the conditions researchers used in a controlled trial with medical supervision. They aren't instructions.
Doses found
Doses as found in each source, with its grade. What was found, not a direction.
Studies, trials and professional sources
n/a
Reddit, Facebook, Instagram, forums and blogs
n/a
Claims and grades
- Not gradedGNT0004 is being studied in a registered trial: A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular Dystrophy (NCT07856329; PHASE2/PHASE3; RECRUITING; sponsor Genethon; intervention "GNT0004 (1x10e13 vg/kg)" (GENETIC)).
Sources (1)
- A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular Dystrophy (opens in a new tab) · ClinicalTrials.gov · trial-registry · 2026-10-02
Educational reference only — not medical advice.
What people report (anecdote)
CLINICAL DATA (from trials)
Adverse events:
None recorded in our sources.
Effects measured:
Human trials: none found.
ANECDOTE
What people report: anecdote, not evidence
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